Ohio State student Cailin Joyce died after suffering a rare blood disorder caused by the Epstein-Barr virus that “left her ...

Novartis is divulging details from ianalumab’s summertime | Novartis is divulging details from ianalumab’s phase 3 win in a rare autoimmune blood disorder, and the data suggest the treatment could del ...

What if we could repair fundamental parts of our bodies? Gene therapy promises just that. It's like having a molecular mechanic that can fix or replace faulty genes, potentially curing diseases ...

Noncancerous blood disorders are conditions that affect blood cells, such as red blood cells, white blood cells, and platelets. Blood disorders may cause symptoms and complications, but most are ...

Sanofi’s Enjaymo, the only approved drug therapy for a rare and debilitating blood disorder, is being acquired by Recordati in a deal that helps the Italian company build its rare disease portfolio ...

Today's biomedical researchers are relentlessly searching for genes that drive disease, with the goal of creating therapies ...

It’s now possible to treat inherited blood diseases, such as sickle cell disease, with gene editing. Blood stem cells are extracted from the patient, modified, and infused back into their bone ...

Exa-cel is the first FDA-approved therapy utilizing CRISPR/Cas9, a type of gene editing technology through which patients' ...

Vertex Pharmaceuticals said on Saturday its gene therapy helped children aged between 5 and 11 years with sickle cell disease ...

A new blood test uses a portable diagnostic system to detect various different diseases in just 15 minutes. The test could change the way we diagnose a wide range of infectious diseases. Here's what ...

Alzheimer's disease is the most common form of dementia worldwide and continues to be one of the greatest public health ...

High blood pressure is not considered a type of heart disease, but it does play a major role in the development of heart disease. High blood pressure (also called hypertension) is one of the biggest ...