RNA-based therapeutics use RNA as a blueprint that enables cells to produce specific proteins—including proteins that can ...

The failure of “del-desiran,” which Novartis got through a $12 billion acquisition, could raise questions about the company’s ...

A new study led by Francesca Storici, a professor in the School of Biological Sciences and faculty member of the Parker H.

Researchers at UC San Diego have demonstrated that a key cellular enzyme can accurately read an eight-letter genetic alphabet ...

Imagine doctors could understand exactly which cells caused a patient's cancer or whether pathogens contributed to the ...

Scientists have identified a previously unrecognized layer of the human genome. It’s built not ...

Researchers at the University of Toronto have developed a next-generation RNA therapeutic approach with the potential to ...

RNA-based vaccines and therapeutics may have faced a bumpy road in the U.S. recently, but a major new federal investment proves the government is still betting big on its future. | RNA-based vaccines ...

The FDA approves zilganersen, the first disease-modifying Alexander disease therapy, offering rare disease developers a trial ...

Chemical and genetic suppression of a microRNA helped prevent disease in mouse models of pulmonary arterial hypertension, ...

A team led by Harvard Medical School (HMS) researchers is exploring the possibility of creating an entire new class of ...