“And we’re off!” celebrated Jon Wood and Anna Wood on Monday morning at home in Grantown as work began on a very special ...
PHILADELPHIA, PA — A rare-disease gene therapy developed in Philadelphia has cleared a major regulatory hurdle, positioning ...
A baby could only have months to live after his family were given a devastating diagnosis. Arthur Hughes, who will turn one ...
Archie was born with a rare condition and was treated in Glasgow Children's Hospital before being transferred to London to ...
Little Archie, from Inverness, was diagnosed with Ornithine Transcarbamylase Deficiency, an extremely rare condition which ...
iECURE, Inc., a genome editing company focused on the development of variant-agnostic in vivo targeted gene insertion therapies for the treatment of liver disorders with significant unmet need, today ...
PHILADELPHIA, January 07, 2026--(BUSINESS WIRE)--iECURE, Inc., a genome editing company focused on the development of variant-agnostic in vivo targeted gene insertion therapies for the treatment of ...
A little Brisbane girl whose every day was once controlled by a debilitating disorder is now living a “calmer, happier” life ...
The liver is the body's control tower for metabolism, powering vital functions like converting nutrients to glucose, storing fat and breaking down toxins. Over a third of the world, however, is ...